Rare Disease
Clinical Research Considerations For Rare Disease Patients: Part 1 — Reinvigorate Patient Centricity
Posted in: Rare Disease, Thought Leadership
The article emphasizes the need for a shift towards patient-centric approaches in […]
Read More....Clinical Research Considerations For Rare Disease Patients: Part 2 — The Impact Of Physician And Site Support
Posted in: Rare Disease, Thought Leadership
Physician and site support are critical for the success of rare disease […]
Read More....High-Velocity Development: Gene Therapy Vs. Small Molecule
Posted in: Rare Disease, Thought Leadership
Gene therapy development operates at a high velocity compared to small molecule […]
Read More....Rare Disease Clinical Endpoints: Ingenuity Meets Practicality
Discover why the science that brought you to this point can only […]
Read More....Rare Disease Clinical Endpoints: Ingenuity Meets Practicality
Discover why the science that brought you to this point can only […]
Read More....Natural History Studies in Gene Therapy Trials: Benefits, Timing and Execution
Natural history studies (NHS) in gene therapy trials are essential for understanding […]
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